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Orchard Therapeutics Announces Publication in The Lancet of Long-term Clinical Outcomes with Libmeldy for the Treatment of Children with Early-onset MLD

Metachromatic Leukodystrophy (MLD)

https://ir.orchard-tx.com/news-releases/news-release-details/orchard-therapeutics-announces-publication-lancet-long-term

Publication in the Lancet: Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access
https://www.thelancet.com/journals/lancet/article/PIIS0140-6736(21)02017-1/fulltext