Posted on 19th June 2026

Experimental gene therapy for Cockayne Syndrome

New York City Child Becomes First Patient Treated With Gene Therapy for Cockayne Syndrome

A 6-year-old Riaan has received an experimental gene therapy for Cockayne Syndrome at New York-Presbyterian Komansky Children’s Hospital in April.

To find out more about Cockayne Syndrome visit our condition page

To read the full press release: Riaan Research press release