This page provides information about current clinical and observational trials for different types of leukodystrophy. Clinical trials, also known as interventional trials, is where there is a medical treatment or intervention assigned to the participant based on the protocol, this may also include placebos. Observational trials are when participants observed and their health outcomes are investigated, but there is no medical treatment or intervention assigned to them. This includes natural history studies and patient registries.
You can ask your doctor or patient organisation such as Alex TLC if they know about clinical trials, natural history studies and patient registries that you would be eligible for.
This includes current clinical trials that are recruiting patients.
You can ask your doctor or patient organisation such as Alex TLC if they know about clinical trials that you would be eligible for. You can contact us at info@alextlc.org
Last checked 29.04.25
This includes current clinical trials that are enrolling patients by invitation only.
You can ask your doctor or patient organisation such as Alex TLC if they know about clinical trials that you would be eligible for. You can contact us at info@alextlc.org
Last checked 29.04.25
This includes current clinical trials that are actively running and are not recruiting more patients.
You can ask your doctor or patient organisation such as Alex TLC if they know about clinical trials that you would be eligible for. You can contact us at info@alextlc.org
Last checked 29.04.25
This includes current natural history studies that are actively running and are recruiting patients.
You can ask your doctor or patient organisation such as Alex TLC if they know about clinical trials that you would be eligible for. You can contact us at info@alextlc.org
Last checked 29.04.25
This includes current natural history studies that are actively running and are not recruiting more patients.
You can ask your doctor or patient organisation such as Alex TLC if they know about clinical trials that you would be eligible for. You can contact us at info@alextlc.org
Last checked 29.04.25
This includes current patient registries that are actively running and are recruiting patients.
You can ask your doctor or patient organisation such as Alex TLC if they know about clinical trials that you would be eligible for. You can contact us at info@alextlc.org
Last checked 29.04.25
There are also websites with information on clinical trials where you can search for information and register your interest, including:
Global Leukodystrophy Initiaitve Clinical Trials Network (GLIA-CTN) Online Referral Survey
WHO International Clinical Trials
You may come across different study types while searching, to find out more about them please visit our research page.
