Guanabenz Trial

Guanabenz Trial for Vanishing White Matter Disease (VMWD)

Therapeutic trial in patients with early-childhood onset vanishing white matter has opened in Amsterdam.
The objective of the trial is to ‘evaluate the safety and tolerability profile of guanabenz in pediatric patients with VWM’.
Please see website for further information, including inclusion criteria:
Alex - The Leukodystrophy Charity