Gene Therapy Trials for Krabbe & GM1 gangliosidosis

Passage Bio are openly recruiting for two gene therapy trials
– Early onset and late onset infantile GM1 gangliosidosis
Clinical trial information, including eligibility criteria: https://clinicaltrials.gov/ct2/show/NCT04713475
Register interest for participation in trial:
– Early Infantile Krabbe Disease
Clinical trial information, including eligibility criteria: https://clinicaltrials.gov/ct2/show/NCT04771416
Register interest for participation in trial:
If you have any questions, please contact patientservices@passagebio.com
