Patient-focused drug development meeting for CTX

Patient-focused drug development meeting for CTX

For the first time, people living with CTX and those who care for and about them are invited to share their experiences with the people who research, develop, and regulate treatments for CTX.

On September 14, 2021 from 11:00 AM – 3:00 PM Eastern time, the first patient-focused drug development (PFDD) meeting dedicated to CTX will be held VIRTUALLY. Participants from across the globe are invited to take part.

The United Leukodystrophy Foundation and the CTX community have joined together to make sure FDA staff, drug and medical device developers, and other stakeholders hear directly from people living with CTX about the many burdens of the condition and the treatment outcomes that matter most to them.

YOU can be part of this ground-breaking initiative!


You can learn more about it at

Alex - The Leukodystrophy Charity